Transforming LGMD through Pioneering Gene Therapies

Myonexus Therapeutics is a clinical-stage gene therapy company

Leading Edge

Myonexus Therapeutics in the News

Myonexus Therapeutics Receives Orphan Drug Designation for MYO-102, an Investigational Gene Therapy for Alpha-sarcoglycanopathy (LGMD2D) 150 150 Myonexus Therapeutics

Myonexus Therapeutics Receives Orphan Drug Designation for MYO-102, an Investigational Gene Therapy for Alpha-sarcoglycanopathy (LGMD2D)

NEW ALBANY, Ohio, January 2, 2019 — Myonexus Therapeutics, announced today that the United States Food and Drug Administration (FDA) has granted Orphan Drug Designation…

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Myonexus Therapeutics Announces the Initiation of a Trial for the First-Ever Gene Therapy for Betasarcoglycanopathy, Also Known as Limb-Girdle Muscular Dystrophy Type 2E 150 150 Myonexus Therapeutics

Myonexus Therapeutics Announces the Initiation of a Trial for the First-Ever Gene Therapy for Betasarcoglycanopathy, Also Known as Limb-Girdle Muscular Dystrophy Type 2E

First-in-human trial of MYO-101 based on promising pre-clinical results offering the first corrective approach for LGMD2E NEW ALBANY, Ohio, November 8, 2018 — Myonexus Therapeutics,…

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Myonexus Therapeutics Receives FDA Rare Pediatric Drug Designation for Pioneering Treatment of Limb Girdle Muscular Dystrophy Type 2E 150 150 Myonexus Therapeutics

Myonexus Therapeutics Receives FDA Rare Pediatric Drug Designation for Pioneering Treatment of Limb Girdle Muscular Dystrophy Type 2E

Rare Pediatric Disease Designation for MYO-101 Program Reflects Compelling Data and Enables Priority Review Voucher Eligibility NEW ALBANY, Ohio–(BUSINESS WIRE)–Myonexus Therapeutics, a clinical-stage gene therapy…

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Our Mission

Myonexus Therapeutics is a clinical-stage gene therapy company developing first-ever corrective gene therapies for Limb-Girdle muscular dystrophies, debilitating rare diseases with no treatments.  

Positively Transforming Lives

Myonexus Therapeutics is developing first ever gene treatments for Limb-girdle muscular dystrophy (LGMD) types 2D, 2B, 2E, 2L, and 2C.